Sabrina Paganoni

Company: Massachusetts General Hospital and Harvard Medical School

Job title: Co-Director, Neurological Clinical Research Institute

Seminars:

Advancing ALS Drug Development Through the HEALEY ALS Platform Trial: Accelerating Innovation & Collaboration 8:00 am

Highlighting the design and success of the HEALEY ALS Platform Trial in streamlining drug development and improving trial efficiency through a shared infrastructure Discussing insights from completed and ongoing regimens, including biomarker discoveries, trial outcomes, and implications for ALS treatment strategies Exploring the collaborative framework of the platform, fostering partnerships between academia, industry, and patient…Read more

day: Conference Day One

Panel Discussion: Strategic Funding & Resource Allocation in ALS Research: Overcoming Barriers to Clinical Development 8:30 am

ALS trials are highly resource-intensive, with significant financial and logistical demands, creating a major barrier for therapies entering development Strategies like synthetic control arms, remote visits, and digital biomarkers can cut costs and reduce patient burden, though validation of these technologies remains a challenge Investors prioritize ALS programs with unique therapeutic approaches, including gene therapy…Read more

day: Conference Day One